Danon disease is a rare genetic disorder with three distinct characteristics that affect boys more severely than girls. Can you correctly identify the three main features of Danon disease? Take the quiz to...
A 2-year-old boy presents with his parents to a pediatric clinic. He had previously been diagnosed with hypospadias. His parents explain that he has been showing symptoms of troubled breathing, excessive...
A recent study on gene therapy for Danon disease revealed findings related to its impact on the condition’s hallmark cardiac pathology. What finding suggested the therapy could effectively target the...
